Synthetic triglyceride shows potential in Huntington’s diseaseSeptember 23, 2021Rare DiseasesNeuromuscular Disorders
Basal ganglia microcircuits offer clues to Parkinson’s symptomsApril 30, 2021Parkinson's DiseaseNeuromuscular Disorders
Neurologic disorders ubiquitous and rising in the U.S.March 2, 2021Alzheimer's & CognitionEpilepsy & SeizuresHeadache & MigraineMovement DisordersMultiple SclerosisNeuromuscular DisordersParkinson's Disease
FDA approves first targeted treatment for rare DMD mutationFebruary 26, 2021Rare DiseasesPediatricsNeuromuscular Disorders
New steroid dosing regimen for myasthenia gravisFebruary 19, 2021Rare DiseasesNeuromuscular Disorders
Joint guidelines favor antibody testing for certain Lyme disease manifestationsDecember 8, 2020PainNeuromuscular DisordersMultiple Sclerosis
Gene-replacement therapy shows promise in X-linked myotubular myopathyNovember 5, 2020Neuromuscular DisordersRare Diseases
Ataluren delays disease milestones in patients with nonsense mutation DMDOctober 27, 2020Rare DiseasesPediatricsNeuromuscular Disorders
Acute flaccid myelitis: More likely missed than diagnosedOctober 26, 2020Neuromuscular DisordersPediatrics
Nusinersen provides continued benefits to presymptomatic children with SMAOctober 22, 2020Rare DiseasesPediatricsNeurodevelopmental DisordersNeuromuscular Disorders
FDA approves viltolarsen (Viltepso) for Duchenne muscular dystrophyAugust 13, 2020Rare DiseasesNeurodevelopmental DisordersNeuromuscular Disorders
FDA expands Dysport use for cerebral palsy–related spasticityJuly 13, 2020Neuromuscular DisordersPediatrics
First reported U.S. case of COVID-19 linked to Guillain-Barré syndromeJune 24, 2020COVID-19 UpdatesRare DiseasesNeuromuscular Disorders