CDC warns of enterovirus strain linked to polio-like conditionSeptember 13, 2022PediatricsRare Diseases
Expected spike in acute flaccid myelitis did not occur in 2020November 8, 2021Neuromuscular DisordersPediatricsRare Diseases
First case of COVID-19 presenting as Guillain-Barré reportedApril 9, 2020COVID-19 UpdatesRare DiseasesNeuromuscular Disorders
Eculizumab reduces relapse-related hospitalizations in patients with NMOSDFebruary 29, 2020Rare DiseasesMultiple Sclerosis
Zika virus: Birth defects rose fourfold in U.S. hardest-hit areasJanuary 27, 2020PediatricsRare Diseases
Expedited review programs not shortening drug developmentJanuary 14, 2020Business of MedicineRare Diseases
Study delineates spectrum of Dravet syndrome phenotypesDecember 10, 2019Epilepsy & SeizuresRare Diseases
Reduction in convulsive seizure frequency is associated with improved executive function in Dravet syndromeDecember 10, 2019Epilepsy & SeizuresRare Diseases
AVXS-101 may result in long-term motor improvements in SMANovember 18, 2019Rare DiseasesPediatricsNeuromuscular Disorders