FDA approves Zolgensma for infantile-onset SMA treatmentMay 24, 2019Rare DiseasesPediatricsGene Therapy
New brain circuitry found with Parkinson’s disease gene therapyNovember 28, 2018Movement DisordersParkinson's DiseaseGene Therapy
Investigational gene therapy for medically refractory Parkinson’s shows promiseOctober 29, 2018Movement DisordersParkinson's DiseaseNeurosurgery & TraumaGene Therapy
Spinal muscular atrophy added to newborn screening panel recommendationsJuly 18, 2018PediatricsNeuromuscular DisordersGene Therapy
Payers part of the drug-pricing problem, says FDA commissionerMarch 7, 2018Business of MedicineGene Therapy
Experts call for international cooperation on human gene editingDecember 3, 2015PediatricsRare DiseasesGene Therapy
