Nanoparticle shows promise for ALSApril 6, 2022Rare DiseasesNeuromuscular DisordersMovement Disorders
Brain implant is a potential life-changer for paralyzed patientsApril 6, 2022TraumaRare DiseasesNeurosurgery & Trauma
Novel drug significantly reduces tics in Tourette syndrome – without side effectsApril 4, 2022PediatricsRare DiseasesMovement Disorders
FDA advisory panel rejects new ALS drugMarch 31, 2022Rare DiseasesNeuromuscular DisordersMovement Disorders
New MIS-C guidance addresses diagnostic challenges, cardiac careFebruary 22, 2022COVID-19 UpdatesPediatricsRare Diseases
Giant cell arteritis fast-track clinics pave way for greater ultrasound use in U.S.December 7, 2021Rare Diseases
Synthetic triglyceride shows potential in Huntington’s diseaseSeptember 23, 2021Rare DiseasesNeuromuscular Disorders
Friedreich’s ataxia treatment shows extended benefitSeptember 21, 2021Rare DiseasesMovement Disorders