Omnibus Spending Bill Includes Provisions Important to the Rare Disease CommunityJanuary 8, 2016Rare Diseases
Rare Disease Community Prepares for Worldwide Observance of Rare Disease DayJanuary 8, 2016Rare Diseases
Subtly elevated maternal glucose linked to increased risk of tetralogy of FallotJanuary 7, 2016DiabetesRare DiseasesCardiologyEndocrinology
Study lays groundwork for autologous nerve cell transplantation in Hirschsprung diseaseJanuary 1, 2016GastroenterologyRare Diseases
Smith-Magenis Syndrome (SMS) Research Symposium to Take Place February 4-5December 11, 2015Rare Diseases
Video: Eltrombopag boosted standard therapy in severe, newly-diagnosed aplastic anemiaDecember 8, 2015HematologyRare Diseases
ASH: Genes affecting risk, severity of chronic ITP are identifiedDecember 6, 2015HematologyRare Diseases
VIDEO: Gene therapy repairs immune function in older patients with SCID-XIDecember 6, 2015HematologyRare Diseases
ASH: Gene therapy restores immune function to older children with SCID-X1December 5, 2015Rare Diseases
