Gene-replacement therapy shows promise in X-linked myotubular myopathyNovember 5, 2020Rare DiseasesNeurologyMusculoskeletal Disorders
JIA arthritis and uveitis flares ‘often run parallel’October 26, 2020Musculoskeletal DisordersRare Diseases
Acute flaccid myelitis: More likely missed than diagnosedOctober 26, 2020NeurologyMusculoskeletal Disorders
Nusinersen provides continued benefits to presymptomatic children with SMAOctober 22, 2020Rare DiseasesNeurologyMusculoskeletal Disorders
New lupus classification criteria perform well in children, young adultsOctober 8, 2020Musculoskeletal DisordersDermatology
Golimumab approval extended to polyarticular-course JIA and juvenile PsAOctober 2, 2020Rare DiseasesMusculoskeletal Disorders
Orthopedic problems in children can be the first indication of acute lymphoblastic leukemiaSeptember 30, 2020OncologyMusculoskeletal Disorders
FDA adds polyarticular-course JIA to approved indications for tofacitinibSeptember 30, 2020Rare DiseasesMusculoskeletal Disorders
Vitamin D pearlsAugust 28, 2020COVID-19 UpdatesDiabetesMusculoskeletal DisordersCardiologyObesityInfectious Diseases
Canakinumab (Ilaris) tapering tested in systemic JIA trialAugust 19, 2020Rare DiseasesMusculoskeletal Disorders
FDA approves viltolarsen (Viltepso) for Duchenne muscular dystrophyAugust 13, 2020Rare DiseasesMusculoskeletal Disorders
ACR issues guidances for MIS-C and pediatric rheumatic disease during pandemicJune 23, 2020COVID-19 UpdatesMusculoskeletal DisordersAdolescent Medicine
Protective levels of vitamin D achievable in SCD with oral supplementationMay 12, 2020HematologyMusculoskeletal Disorders
Expert discusses red flags for interstitial lung disease in pediatric rheumatologyMay 6, 2020Rare DiseasesMusculoskeletal DisordersPulmonology