Neurology ReviewsAVXS-101 may result in long-term motor improvements in SMANovember 18, 2019Rare DiseasesPediatricsNeuromuscular Disorders
Clinical Neurology NewsAtaluren shows real-world benefit for nonsense mutation Duchenne muscular dystrophyNovember 7, 2019Neuromuscular DisordersRare Diseases
Neurology ReviewsFamilies face challenges of gene therapyNovember 5, 2019Rare DiseasesGene TherapyPediatrics
Neurology ReviewsExperts address barriers to genetic screeningNovember 4, 2019Rare DiseasesPediatrics
Clinical Neurology NewsCMT1A neuropathy improves with investigational drug PXT3003October 29, 2019Neuromuscular DisordersRare Diseases
Neurology ReviewsBaricitinib may benefit patients with Aicardi-Goutières syndromeOctober 28, 2019Rare DiseasesPediatrics
Neurology ReviewsNeurologists publish consensus statement on stridor in MSAOctober 15, 2019Rare DiseasesSleep MedicineNeuromuscular Disorders
Neurology ReviewsC-Path and NORD team up to speed development of treatments for rare disordersOctober 7, 2019Rare Diseases
Clinical Neurology NewsCerliponase alfa continues to impress for CLN2 diseaseAugust 30, 2019PediatricsRare Diseases
Clinical Neurology News‘Pot’ is still hot for Dravet, Lennox-GastautAugust 22, 2019Epilepsy & SeizuresRare DiseasesPediatrics
Clinical Neurology NewsPossible role of enterovirus infection in acute flaccid myelitis cases detectedAugust 14, 2019Rare DiseasesPediatrics
Clinical Neurology NewsNIH launches 5-year, $10 million study on acute flaccid myelitisJuly 25, 2019PediatricsRare DiseasesNeuromuscular Disorders
Neurology ReviewsStudy refines ALS risk among first-degree relatives of patients with diseaseJuly 23, 2019Neuromuscular DisordersRare Diseases
Clinical Neurology NewsCDC: Look for early symptoms of acute flaccid myelitis, report suspected casesJuly 9, 2019PediatricsRare Diseases
Neurology ReviewsFDA approves first treatment for neuromyelitis optica spectrum disorderJune 27, 2019Rare Diseases
