Neurology ReviewsAtaluren delays disease milestones in patients with nonsense mutation DMDOctober 27, 2020Rare DiseasesPediatricsNeuromuscular Disorders
Neurology ReviewsNusinersen provides continued benefits to presymptomatic children with SMAOctober 22, 2020Rare DiseasesPediatricsNeurodevelopmental DisordersNeuromuscular Disorders
Neurology ReviewsCBD for LGS: Fewer seizures, but thrombocytopenia riskOctober 22, 2020Epilepsy & SeizuresRare DiseasesPediatrics
Neurology ReviewsNMOSD challenges in childrenOctober 21, 2020Rare DiseasesMultiple SclerosisPediatrics
Neurology ReviewsDrug combo slows functional decline in ALSSeptember 8, 2020Rare DiseasesNeuromuscular Disorders
Neurology ReviewsTNF inhibitors linked to inflammatory CNS eventsAugust 25, 2020Rare DiseasesMultiple Sclerosis
Neurology ReviewsCOVID-19 linked to development of myasthenia gravisAugust 21, 2020COVID-19 UpdatesRare Diseases
Neurology ReviewsFDA approves viltolarsen (Viltepso) for Duchenne muscular dystrophyAugust 13, 2020Rare DiseasesNeurodevelopmental DisordersNeuromuscular Disorders
Neurology ReviewsFDA approves first oral treatment for spinal muscular atrophyAugust 11, 2020Rare DiseasesPediatrics
Neurology ReviewsPsychiatrists report rare case of woman who thinks she’s a chicken July 31, 2020Epilepsy & SeizuresRare Diseases
Neurology ReviewsFDA approves new treatment for Dravet syndromeJune 26, 2020Epilepsy & SeizuresRare Diseases
Neurology ReviewsFirst reported U.S. case of COVID-19 linked to Guillain-Barré syndromeJune 24, 2020COVID-19 UpdatesRare DiseasesNeuromuscular Disorders
Neurology ReviewsHuntington’s disease biomarkers appear 24 years before clinical symptomsJune 5, 2020Rare DiseasesNeuromuscular DisordersMovement Disorders
Neurology ReviewsNew research confirms the efficacy and safety of onasemnogene abeparvovec for SMAMay 19, 2020Rare DiseasesPediatrics
