FDA approves afamelanotide for treatment of rare condition with light-induced painOctober 8, 2019Rare DiseasesDermatologyPain
C-Path and NORD team up to speed development of treatments for rare disordersOctober 7, 2019Rare DiseasesNeurology
mIDH1 inhibitor ivosidenib improves progression-free survival in advanced cholangiocarcinomaOctober 1, 2019Rare Diseases
USPSTF: Screening pregnant women for asymptomatic bacteriuria cuts pyelonephritis riskSeptember 24, 2019Women's HealthInfectious DiseasesNephrologySexual HealthRare Diseases
New genotype of S. pyrogenes found in rise of scarlet fever in U.K.September 10, 2019Infectious DiseasesRare Diseases
Disseminated Invasive Candidiasis in an Immunocompetent HostSeptember 3, 2019Hospital MedicineRare Diseases
Favorable Ebola results lead to drug trial termination, new focusAugust 12, 2019Infectious DiseasesRare Diseases
Treatment Facility: An Important Prognostic Factor for Dedifferentiated Liposarcoma Survival (FULL)August 8, 2019OncologyRare DiseasesMixed Topics
FDA advisors recommend nintedanib for SSc interstitial lung diseaseJuly 26, 2019PulmonologyRare Diseases