The Latest in Rare Diseases

Long-acting pasireotide approved for acromegaly

December 18, 2014

FDA approves newborn screening test for SCID

December 16, 2014

Rare Diseases

Autism sibling studies beginning to yield data

August 25, 2014

Economic cost of autism disorders is considerable

June 9, 2014

Gene panel identifies residual neuroblastoma metastases

January 7, 2014

Resurrected gemtuzumab shows benefit against pediatric AML

December 9, 2013