FDA approves first Erdheim-Chester disease treatmentNovember 6, 2017Rare DiseasesLeukemia, Myelodysplasia, Transplantation
Orphan Drugs Are Not Driving Up the Cost of Health Care, According to New StudyNovember 1, 2017Rare Diseases
PSC Partners Seeking a Cure Surpasses 1,000 Patients in International Registry … and Makes an Unexpected Finding Regarding MisdiagnosisSeptember 27, 2017Rare Diseases