GAO to launch investigation of FDA’s Orphan Drug programMarch 22, 2017Rare DiseasesBusiness of Medicine
Large, intermittent vitamin D doses may increase fracture, fall risk in elderlyMarch 3, 2017GeriatricsRare DiseasesMusculoskeletal DisordersRheumatology
Pediatric lupus patients face large burden of serious infectionFebruary 27, 2017Rare DiseasesRheumatology
Guidelines tackle long-term screening, management of myelomaFebruary 25, 2017OncologyHematologyRare Diseases
Lanadelumab reduced hereditary angioedema attacks by 88%-100%February 22, 2017ImmunologyRare DiseasesPulmonologyHematology
Foundation for Prader-Willi Research Highlights Study of Genetic Therapy for Prader-Willi SyndromeFebruary 17, 2017Rare Diseases
