WASHINGTON – Most patients with opsoclonus myoclonus syndrome experience ataxia, among multiple other symptoms.
Inotersen inhibits the production of amyloid in patients with the rare disorder.
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And beware a nasty skin souvenir from travel abroad.
LAKE TAHOE, CALIF. – Mosaicism “can affect any tissue, anywhere, in any pattern,” expert says.
A pivotal phase 2/3 trial of bertilimumab will begin next year, according to the company.