Drug nets orphan designation for SCD

The European Commission (EC) has granted orphan designation to Altemia (formerly SC411) for the treatment of pediatric patients with sickle cell...

Conference Coverage

Phase 1 results with UCART19 in kids

LISBON—Early results from a phase 1, pediatric trial of UCART19 expand upon results observed in children who received the therapy via a...

Conference Coverage

AdV viral burden linked to mortality in kids

LISBON—Data from the AdVance study revealed a “strong correlation” between adenovirus (AdV) viral load and mortality in pediatric recipients of...