Pediatric NewsFenfluramine trials in Dravet syndrome yield highly positive resultsDecember 6, 2017Rare DiseasesNeurology
Pediatric NewsMorgan Leary Vaughan Fund Receives Petit Family Foundation GrantNovember 2, 2017Rare Diseases
Pediatric NewsSmall Kansas Town Turns Night Into Day for Boy With Rare DiseaseNovember 1, 2017Rare Diseases
Pediatric NewsNORD Board Chair to Moderate Social Security Administration ForumNovember 1, 2017Rare Diseases
Pediatric NewsOrphan Drugs Are Not Driving Up the Cost of Health Care, According to New StudyNovember 1, 2017Rare Diseases
Pediatric NewsNominate a Colleague or Patient for a NORD Rare Impact AwardNovember 1, 2017Rare Diseases
Pediatric NewsGene therapy for cerebral adrenoleukodystrophy shows promiseOctober 9, 2017Rare DiseasesNeurology
Pediatric NewsBiologic may bring relief for children and adults with XLH syndromeOctober 2, 2017EndocrinologyRare Diseases
Pediatric NewsVestibular Disorders Association Celebrates Balance Awareness WeekSeptember 27, 2017Rare Diseases
Pediatric NewsPSC Partners Seeking a Cure Surpasses 1,000 Patients in International Registry … and Makes an Unexpected Finding Regarding MisdiagnosisSeptember 27, 2017Rare Diseases
Pediatric NewsFoundation Fighting Blindness Opens USH2A Natural History StudySeptember 27, 2017Rare Diseases