Pediatric NewsNORD Unveils “Do Your Share for Rare” Year-Long Awareness CampaignMarch 29, 2017Rare Diseases
Pediatric NewsGAO to launch investigation of FDA’s Orphan Drug programMarch 22, 2017Rare DiseasesBusiness of Medicine
Pediatric NewsLanadelumab reduced hereditary angioedema attacks by 88%-100%February 22, 2017ImmunologyRare DiseasesPulmonologyHematology
Pediatric NewsFoundation for Prader-Willi Research Highlights Study of Genetic Therapy for Prader-Willi SyndromeFebruary 17, 2017Rare Diseases
Pediatric NewsAplastic Anemia & MDS International Foundation Research Portal Is OpenFebruary 17, 2017Rare Diseases
Pediatric NewsNORD Publishes Report on Spontaneous Intracranial Hypotension (SIH)February 17, 2017Rare Diseases
Pediatric NewsCORD Offers Consensus Framework for Ethical CollaborationFebruary 17, 2017Rare Diseases