Pediatric NewsLosartan showing promise in pediatric epidermolysis bullosa trialFebruary 4, 2020DermatologyRare Diseases
Pediatric NewsHigh cost of wound dressings for epidermolysis bullosa highlightedFebruary 3, 2020Rare DiseasesDermatology
Pediatric NewsMost epidermolysis bullosa patients turn to topical antimicrobialsFebruary 1, 2020Rare DiseasesDermatology
Pediatric NewsZika virus: Birth defects rose fourfold in U.S. hardest-hit areasJanuary 27, 2020ZikaInfectious DiseasesNeurologyRare Diseases
Pediatric NewsExpedited review programs not shortening drug developmentJanuary 14, 2020Business of MedicineRare Diseases
Pediatric NewsADA2 is a potent new biomarker for macrophage activation syndromeDecember 11, 2019Rare DiseasesImmunology
Pediatric NewsTofacitinib improves disease activity in patients with polyarticular-course JIADecember 11, 2019Rare DiseasesMusculoskeletal Disorders
Pediatric NewsAVXS-101 may result in long-term motor improvements in SMANovember 18, 2019Rare DiseasesMusculoskeletal Disorders
Pediatric NewsAtaluren shows real-world benefit for nonsense mutation Duchenne muscular dystrophyNovember 7, 2019Rare Diseases
Pediatric NewsBaricitinib may benefit patients with Aicardi-Goutières syndromeOctober 28, 2019Rare DiseasesNeurology
Pediatric NewsFDA approves rituximab to treat children with rare vasculitisSeptember 30, 2019Rare DiseasesMixed Topics
Pediatric NewsAnakinra treatment for pediatric ‘cytokine storms’: Does one size fit all?September 25, 2019Rare DiseasesImmunology