Medical Education Library

Fundamentals of Gene Therapy: Addressing Gaps in Physician Education

This supplement is sponsored by uniQure B.V.


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Gene therapy is a contemporary therapeutic intervention with recent positive results and regulatory approvals either completed or expected in the next several years for various con­ditions. In this supplement, learn more about:

  • Basic principles of gene therapy
  • In vivo vs ex vivo methods of gene transfer
  • Vector types
  • Clinical Considerations

About the Author

John Pasi, MB, ChB, PhD
Professor of Haemostasis and Thrombosis
Barts and The London School of Medicine and Dentistry
Haemophilia Centre
London, UK

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