Bleeding Disorders

News

Drug gets orphan status for PNH in US

The US Food and Drug Administration (FDA) has granted the complement inhibitor AMY-101 orphan status as a treatment for paroxysmal nocturnal...

News

New approach for treating PNH

Investigators have identified a novel strategy for treating paroxysmal nocturnal hemoglobinuria (PNH), according to a paper published in Blood....

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Inhibitor strengthens RBCs in PNH

Credit: NHLBI The apoptosis inhibitor aurin tricarboxylic acid (ATA) is active against paroxysmal nocturnal hemoglobinemia (PNH), according to...

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