Pediatric NewsGenomic screening of healthy newborns gets more popularDecember 2, 2021Neonatal MedicineRare DiseasesOncology
Pediatric NewsDrug combo at outset of polyarticular JIA benefits patients mostNovember 10, 2021Rare DiseasesMusculoskeletal Disorders
Pediatric NewsExpected spike in acute flaccid myelitis did not occur in 2020November 8, 2021Infectious DiseasesRare DiseasesNeurology
Pediatric NewsEvaluations of novel approaches to treating NF-1 tumors are underwayOctober 29, 2021Rare DiseasesDermatology
Pediatric NewsClinical genetic testing for skin disorders continues to advanceSeptember 8, 2021Rare DiseasesDermatology
Pediatric NewsTargeted therapies for vascular anomalies continue to be refinedSeptember 3, 2021DermatologyRare Diseases
Pediatric NewsFDA approves first once-weekly growth hormone for childrenSeptember 3, 2021EndocrinologyRare Diseases
Pediatric NewsStudy informs about risks of discontinuing meds in JIAAugust 25, 2021Rare DiseasesMusculoskeletal Disorders
Pediatric NewsFDA approves new enzyme replacement therapy for Pompe diseaseAugust 11, 2021Rare Diseases
Pediatric NewsGenetic testing for neurofibromatosis 1: An imperfect scienceJuly 27, 2021DermatologyRare Diseases
Pediatric NewsAutoinflammatory diseases ‘not so rare after all,’ expert saysJuly 22, 2021DermatologyRare Diseases
Pediatric NewsNovel gene therapy ‘reprograms’ cells to reverse neurologic deficits in children with rare diseaseJuly 22, 2021Rare DiseasesNeurology
Pediatric NewsU.S., international MIS-C studies yield disparate resultsJune 18, 2021COVID-19 UpdatesInfectious DiseasesRare DiseasesCardiologyPulmonologyImmunology
Pediatric NewsSecukinumab provides clinical benefit in phase 3 juvenile arthritis trialJune 15, 2021Rare DiseasesMusculoskeletal Disorders
Pediatric NewsEULAR, ACR present preliminary recommendations for rare genetic autoinflammatory diseasesJune 5, 2021Rare Diseases